leisure time -WSS

leisure time

author：entertainment 2025-10-02 21:07:17 - browse：986

Seng Cheng has been working in gene therapy for nearly as long as gene therapy has been a field. As a young scientist in the early 1990s, he was part of one of three teams racing to develop a gene therapy for cystic fibrosis, a high-profile effort that resulted in national headlines, prestigious publications, and zero patients cured.

So he’s seen the field’s highs and lows. Lately, there have been a lot of both, including at Pfizer, the company Cheng called home until this summer. The pharma brought three potentially powerful gene therapies for muscular dystrophy and hemophilia into late-stage trials but, in January, chose to abandon a large portfolio of early stage candidates that relied on the same technology: adeno-associated viruses, or AAVs, a group of small bugs that scientists spent two decades taming into a gene shipping system.

The move seemed emblematic. Across the industry, AAV companies have been struggling, either shelving programs or stopping work altogether, while investors shuttled money toward new technologies such as CRISPR and its various permutations. Longtime researchers feared promising drugs, particularly for ultra-rare diseases, might get lost in the shuffle.

Get unlimited access to award-winning journalism and exclusive events.

Subscribe Log In

Previous article： Novavax promises a turnaround & Lilly roils the obesity market
Next article： Lindsay Lohan welcomes 1st child with husband Bader Shammas

hotspot

WSS

Readout Newsletter: Novavax stock, FogPharma, Novo Nordisk

Exact Sciences stock tumbles despite strong cancer detection sales

MultiPlan and major insurers sued for alleged medical price

Plane’s emergency slide plummets from sky, hits Chicago home

Medical bills so high, Medicare adding extra digits to claim forms

Ebola public health emergency is over, WHO declares

knowledge

leisure time

focus

As demand for Covid shots wanes, Moderna seeks its next success

Bird flu in milk supply is likely coming from asymptomatic cows

Medical records are filled with copy

MultiPlan and major insurers sued for alleged medical price

Tori Bowie and the unacceptable rates of Black maternal death

Celebrate National Dole Whip Day for 3 days this week at Disney

Continuity nursing helped my family in our darkest PICU moments

Key Senate committee drafts bipartisan bill to stem drug shortages

BioMarin wins approval for gene therapy to treat hemophilia A

FTC falls short on scrutinizing hospital mergers, study says

knowledge

India sets sights on home

Why some people catch Covid but never get sick

Dogs on Prozac: What pet anti

Plane’s emergency slide plummets from sky, hits Chicago home

Celebrate National Dole Whip Day for 3 days this week at Disney

After traumatic brain injury, life support decisions can use more time

explore

focus

hotspot

knowledge