entertainment -WSS

entertainment

author：explore 2025-10-02 13:41:11 - browse：47284

Colorful broken DNA helix genome. -- health coverage from STAT — Adobe

In 2020, as biotech stocks surged amid the pandemic, a startup called Taysha Gene Therapies raised over $300 million off an audacious promise: It was going to license and develop gene therapies for at least 18 different rare and serious neurological diseases.

The effort brought hope for many rare disease families, some of whom had raised money to fund the UT-Southwestern scientist who designed the treatments after they saw no other options for their children.

Last week, the grand plan took perhaps a final blow. Taysha announced it would discontinue development of a treatment for giant axonal neuropathy, or GAN, a fatal, degenerative disease known to affect fewer than 100 people worldwide. The FDA, Taysha said, had requested an additional clinical trial that would be infeasible.

Get unlimited access to award-winning journalism and exclusive events.

Subscribe Log In

Previous article： Guidelines to prevent youth baseball injuries need more muscle
Next article： Illumina names Agilent executive as new CEO

WSS

Amylyx ALS drug fails large clinical trial

IVF, abortion rights issues kick off Biden’s State of the Union

Change Healthcare cyberattack prompts Medicare loan program

CDC marks new Covid

Amazon on where the company's health care bets are headed next

How generative AI is inspiring dreams of a health data revolution

entertainment

entertainment

entertainment

In Memoriam: Notable people who died in 2023

In his State of the Union, Biden takes clear aim at 'Big Pharma'

In age of alternative facts, a scholarly course on calling out crap

Ethical issues complicate the benefits of medical crowdfunding

Medicare details structure of new drug price negotiation program

The (many) problems with a new study criticizing cancer screening

Apple is now the first public company to be valued at $3 trillion

Readout LOUD podcast: Venture capital turmoil, obesity drug competition

Virginia high school admissions case could be legal follow

How to protect patients from sexual assault

hotspot

Sen. Paul opposes bill to ban Chinese biotechs

Amylyx ALS drug fails large clinical trial

Novo Nordisk gets FDA approval to tout heart benefits of Wegovy

Seth Rogen and Lauren Miller Rogen on Alzheimer's caregiving

How generative AI is inspiring dreams of a health data revolution

CDC marks new Covid

leisure time

hotspot

hotspot

hotspot