fashion -WSS

fashion

author：comprehensive 2025-09-30 20:47:20 - browse：5

Colorful broken DNA helix genome. -- health coverage from STAT — Adobe

In 2020, as biotech stocks surged amid the pandemic, a startup called Taysha Gene Therapies raised over $300 million off an audacious promise: It was going to license and develop gene therapies for at least 18 different rare and serious neurological diseases.

The effort brought hope for many rare disease families, some of whom had raised money to fund the UT-Southwestern scientist who designed the treatments after they saw no other options for their children.

Last week, the grand plan took perhaps a final blow. Taysha announced it would discontinue development of a treatment for giant axonal neuropathy, or GAN, a fatal, degenerative disease known to affect fewer than 100 people worldwide. The FDA, Taysha said, had requested an additional clinical trial that would be infeasible.

Get unlimited access to award-winning journalism and exclusive events.

Subscribe Log In

Previous article： In Memoriam: Notable people who died in 2023
Next article： Adam's Biotech Scorecard: A closer look at Viking Therapeutics, PDS Biotech

WSS

Study says nonprofit hospitals fall short in charity care spending

Washington mulls new rules to avert another Change Healthcare

Washington mulls new rules to avert another Change Healthcare

Hospitals are piloting generative AI tools as regulators play catch

States should stop sabotaging methadone treatment reform

Patient advocates debate FDA's accelerated approval process

focus

fashion

focus

Dobbs anniversary: the lost opportunity of abortion as health care

Ukraine seeks to reclaim its role as a hub for clinical trials

Affirmative action in medical school literally saved lives

Why the world’s most expensive drug might be worth the price

Novavax promises a turnaround & Lilly roils the obesity market

Patient advocates debate FDA's accelerated approval process

Peter Hotez and the public health issue of online harassment

Oprah kicked off a national conversation on obesity. Let's have it

George Santos makes 1st court appearance after pleading not guilty to 13 counts

Vertex Pharmaceuticals may move headquarters in Boston

explore

MD Anderson's Padmanee Sharma responds to research credit suit

Food as medicine: Medically tailored meals may get standardized

Abortion pill Supreme Court ruling could impact entire drug industry

Decaf coffee targeted by food safety group under obscure FDA rule

Roche subsidiary Foundation Medicine opens new headquarters

Readout LOUD podcast: Pharma in Washington, Alnylam, and Gilead

knowledge

focus

hotspot

focus