~~<i id='F8AA072340'><strike id='F8AA072340'><tt id='F8AA072340'><pre id='F8AA072340'></pre></tt></strike></i>~~

00:00

00:00 00:00 LIVE

buffering

Replay

hotspot

leisure time

author：fashion 2025-09-30 16:28:53 - browse：7

An illustration of red blood cells — Adobe

As a boy growing up with hemophilia A, Noah Frederick reserved the end of his annual checkups to talk about new technologies. His doctor walked through various experimental approaches for the bleeding disorder and, invariably, gene therapy. It was coming, he always said, in your lifetime.

Last year, it finally arrived. But Frederick, now a 23-year-old software engineer, isn’t sure he’ll get it. He wants to be part of the sci-fi future gene therapy has always represented, but a recent doctor’s visit left him uncertain.

“I’m on the fence,” he said.

Get unlimited access to award-winning journalism and exclusive events.

Subscribe Log In

Previous article： Bright Health sells Medicare Advantage business to Molina
Next article： Readout LOUD podcast: Venture capital turmoil, obesity drug competition

focus

hotspot

entertainment

focus

RaDondaVaughtsitsinacourtroomaheadofhersentencinginNashville,Tenn.,onFriday,May13,2022.NicoleHester/

WSS

WuXi out of biotech trade group, U.S. and China relations to blame

Former medical device CEO who sold dummy, plastic parts convicted of fraud

First medicine developed to treat MASH expected to be approved soon

Sen. Paul opposes bill to ban Chinese biotechs

HHS secretary Becerra pressed on Change HealthCare cyberattack

In his State of the Union, Biden takes clear aim at 'Big Pharma'

hotspot

leisure time

focus

As demand for Covid shots wanes, Moderna seeks its next success

Amylyx ALS drug fails large clinical trial

Medical leaders decry Supreme Court decision on affirmative action

Male and female sex labels in research insufficient, scientists say

Heart attack and stroke risk calculators need revising

Male and female sex labels in research insufficient, scientists say

Tori Bowie and the unacceptable rates of Black maternal death

Boston's new lab space is opening empty

Indiana Supreme Court upholds abortion ban, says state constitution gives only limited protections

Ebola: Gilead Sciences antiviral shows promise as new treatment

focus

How to save health care price transparency rules

Why depression after traumatic brain injury is distinct

What it’s like to watch children die of measles

The Readout: Amylyx, Alumis, and Lundbeck drug updates

Precocious puberty in girls comes with mental health risks

President Biden's budget: Here's what you might have missed

hotspot

hotspot

entertainment

focus