leisure time -WSS

leisure time

author：leisure time 2025-10-01 04:32:50 - browse：891

Gene therapy helped Conner Curran, right, walk, but as the drug fades, his family is supporting scientific efforts to allow him and other boys get a second dose. -- Biotech coverage from STAT — Gene therapy helped Conner Curran (at right) walk, but as the drug fades, his family is supporting scientific efforts to allow him and other boys get a second dose. Courtesy Jess & Chris Curran

In the beginning, Conner Curran ran up the stairs.

It was a miraculous moment for him and his parents, Jess and Chris Curran. Just months before, contractors were in their New York home to install a motorized lift, while Jess tearfully explained that it wasn’t for a grandparent but for their 7-year-old son, who suffered from Duchenne muscular dystrophy and could barely haul himself up the steps.

Then Conner was accepted as the first patient in Pfizer’s Duchenne gene therapy trial. Three weeks later, he could bound to the second floor. Soon, he could walk the two-plus miles to Goldberg’s, a local bagel shop. “I couldn’t do that before,” he told NPR in 2020.

Unlock this article by subscribing to STAT+ and enjoy your first 30 days free!

GET STARTED Log In

Previous article： BioMarin wins approval for gene therapy to treat hemophilia A
Next article： What is artificial intelligence? Experts weigh in

hotspot

WSS

In a test for AI, buzzy startup Insitro inks drug discovery deal with Gilead

Commercial surrogacy can be ethical, despite pope’s claims

Pfizer's RSV vaccine recommended for approval in Europe

Biden, Billy Joel, Elton John lead tributes for Tony Bennett after singer's death at 96

Some dementia cases could be undiagnosed liver disease

Florida babysitter arrested over hot car death, authorities say

entertainment

leisure time

hotspot

Virginia high school admissions case could be legal follow

New chart reveals military’s vast involvement in Operation Warp Speed

Medicare details structure of new drug price negotiation program

Dispute over threat of extinction posed by artificial intelligence looms over surging industry

Jerome Adams on the need for new antivirals for Covid

Family of Gilgo Beach murder suspect releases statement: 'Devastating time'

ChatGPT in medicine: STAT answers readers' burning questions

Novo Nordisk to expand supply of Wegovy for U.S. patients

State Dept. review finds Biden bears some blame for Afghanistan failures

Biden administration opens offers in Medicare drug price negotiations

hotspot

Mega Millions jackpot grows to $720 million ahead of Friday's drawing

The biotech scorecard for the 2nd quarter: 12 industry events to watch

Hey, doctors: Don't be no

Woodcock on FDA’s accelerated approval and her next chapter

Apple Vision Pro: A first look at health apps on the new VR headset

Covid misinformation case heads to Supreme Court

hotspot

entertainment

hotspot

explore