entertainment -WSS

entertainment

author：knowledge 2025-10-01 23:06:34 - browse：17184

The FDA building -- First Opinion coverage from STAT — Adobe

U.S. regulators on Wednesday approved the first treatment for an ultra-rare disease that causes people to grow bone where it otherwise shouldn’t be, extending an option to patients who have been advocating for access to the medicine.

The treatment, an oral medication that will be marketed as Sohonos, faced some questions about the quality of its data, and was rejected earlier this year by European regulators. But in approving the drug for the treatment of fibrodysplasia ossificans progressiva, or FOP, the Food and Drug Administration concluded that Sohonos’ benefits outweigh its risks.

“I just closed my eyes and looked up to the skies, like ‘Thank you, God,’” said Suzanne Hollywood, whose teenage son, Joey, has been receiving the drug in a clinical trial. “It’s far from perfect, but I’m thrilled for my son, for his future, and for the kids getting diagnosed who might not have to experience what others had to.”

Unlock this article by subscribing to STAT+ and enjoy your first 30 days free!

GET STARTED Log In

Previous article： Tori Bowie and the unacceptable rates of Black maternal death
Next article： Oak Street deal isn't the answer to health care's woes

Wikipedia

WSS

Obesity drug from Roche shows promise in early study

WuXi Biologics execs register to lobby as Congress comes for the company

Readout Newsletter: Raw milk, Wegovy tests, Eisai and Biogen

Fertility clinic egg and embryo storage is a disaster

Readout Newsletter: Raw milk, Wegovy tests, Eisai and Biogen

What a koala virus tells us about the human genome

entertainment

entertainment

Wikipedia

Medical records are filled with copy

Brazil's Jair Bolsonaro is barred from running for office until 2030

Medical leaders decry Supreme Court decision on affirmative action

Synthetic human embryos? Researchers say term is overblown

In Memoriam: Notable people who died in 2023

Brazil's Jair Bolsonaro is barred from running for office until 2030

Trump demands the U.S. pay no more for drugs than other countries … again

Here's how to stay safe from wildfire smoke amid reduced air quality

23andMe had bad news about my health. I wish a person had delivered it

Oak Street deal isn't the answer to health care's woes

leisure time

Why H5N1 bird flu is keeping the CDC's top flu scientist awake

What Wagner Group's armed rebellion could mean for Russia's endgame in Ukraine

Oak Street deal isn't the answer to health care's woes

Synthetic human embryos? Researchers say term is overblown

Supreme Court strikes down Biden student loan forgiveness program

Raw milk easy to obtain despite bird flu warning, FDA interstate ban

focus

Wikipedia

Wikipedia

hotspot