comprehensive -WSS

comprehensive

author：leisure time 2025-10-01 02:15:39 - browse：3152

A young boy died in a trial for Pfizer’s experimental gene therapy for Duchenne muscular dystrophy, the company told patient advocates Tuesday.

The boy was enrolled in Daylight, a trial studying the treatment in boys aged 2 or 3. The boy had received the therapy early last year, Pfizer told the advocates in a note posted online by Parent Project Muscular Dystrophy.

Pfizer said the boy died of cardiac arrest, but that it was still working to understand what happened and the exact cause.

STAT+ Exclusive Story

Already have an account? Log in

This article is exclusive to STAT+ subscribers

Unlock this article — plus daily coverage and analysis of the pharma industry — by subscribing to STAT+.

Already have an account? Log in

Monthly

$39

Totals $468 per year

$39/month Get Started

Totals $468 per year

Starter

$30

for 3 months, then $39/month

$30 for 3 months Get Started

Then $39/month

Annual

$399

Save 15%

$399/year Get Started

Save 15%

11+ Users

Custom

Savings start at 25%!

Request A Quote Request A Quote

Savings start at 25%!

2-10 Users

$300

Annually per user

$300/year Get Started

$300 Annually per user

View All Plans

Get unlimited access to award-winning journalism and exclusive events.

Subscribe Log In

Previous article： Sports medicine is finally prioritizing gender equality
Next article： Senator probes 340B programs at Cleveland Clinic, Bon Secours

WSS

Medicare drug price negotiation program allowed for now

Shingles, which affected Dianne Feinstein, is on the rise

After a drawn out lobbying fight, ARPA

Kale crackers and hibiscus tea: My five days on a 'fasting diet'

RSV vaccines may be linked to small increased risk of developing GBS

Menendez indictment could see pharma lose a key ally

Wikipedia

comprehensive

This article is exclusive to STAT+ subscribers

Unlock this article — plus daily coverage and analysis of the pharma industry — by subscribing to STAT+.

hotspot

Novavax promises a turnaround & Lilly roils the obesity market

Medical device lobby: We're tired of waiting on Medicare coverage

Peter Hotez and the public health issue of online harassment

WHO recommends dropping component of many flu vaccines

DIEP, the 'gold standard' of breast reconstruction, is under threat

Flu vaccine offering decent levels of protection this winter, new data show

Guidelines to prevent youth baseball injuries need more muscle

Inequities make cancer less preventable for women: report

The Supreme Court will review a ruling striking down a domestic violence federal gun ban

STAT Virtual Event: How to Increase Diversity in Clinical Trials

hotspot

Listen: Who gets the credit for GLP

Kaiser Permanente unions announce official strike date

How the Dana

Kale crackers and hibiscus tea: My five days on a 'fasting diet'

How to address the problem of discarded donor organs

Researchers use wearables data and AI to predict preterm birth risk

hotspot

entertainment

Wikipedia

explore