entertainment -WSS

entertainment

author：comprehensive 2025-09-29 22:52:06 - browse：2

Two people run on the sugar-phosphate backbone of DNA while holding base pairs — in the lab coverage from STAT — Adobe

LONDON — Widespread genetic testing as well as the development of cutting-edge, customized genetic therapies have opened the door to treating many more inherited conditions than previously possible. A few recent cases, in which bespoke medicines were created for children with exceedingly rare mutations, have raised hopes for furthering the approach.

Now, researchers and government agencies in the U.K. are trying to figure out the nitty-gritty to replicate those early one-off successes for as many patients as possible — what sort of preclinical testing a tailor-made treatment needs to go through before being used, what regulatory thresholds each treatment needs to clear, and how to pay for these therapies.

“A lot of the barriers are no longer scientific — we can make these drugs,” said Matthew Wood, a professor of pediatrics at the University of Oxford. “It’s more about, can we make them at a cost that is reasonable enough? And can we get the regulators to reduce the barriers to doing this so that when a patient shows up, you can actually make a drug quickly enough to benefit that patient, rather than it costing huge amounts of money and taking two or three years to do it?”

Get unlimited access to award-winning journalism and exclusive events.

Subscribe Log In

Previous article： Over 800 arrested across France in 3rd night of riots after fatal police shooting of teen
Next article： A revolution in caring for preterm infants

Wikipedia

WSS

A revolution in caring for preterm infants

A revolution in caring for preterm infants

CDC overhauls leadership of center that led response to Covid

CDC overhauls leadership of center that led response to Covid

Akero's treatment for NASH falls short in cirrhosis study

Some of the ways extreme heat will change life as we know it

Wikipedia

entertainment

focus

Guidelines to prevent youth baseball injuries need more muscle

Kim Kardashian sparks debate on benefits of full

Hepatitis C has a cure — but many Americans still lack access to it

Who are the detained American citizens released from prison in Iran?

In Memoriam: Notable people who died in 2023

Medicare to cover more brain scans related to Alzheimer’s drugs

What does generative AI mean for health care? We asked experts

CDC overhauls leadership of center that led response to Covid

How one medical school became remarkably diverse

The history of OxyContin, told through Purdue Pharma documents

focus

What the Wegovy shortage looks like for doctors — and for patients

Peter Marks talks Operation Warp Speed for Rare Diseases

Maui funeral service workers on devastation of fires: 'I'm in shock'

Some of the ways extreme heat will change life as we know it

GOP presidential candidates start declaring their loyalty

Eight reasons why you should get an updated Covid vaccine

Wikipedia

Wikipedia

leisure time

knowledge