leisure time -WSS

leisure time

author：entertainment 2025-09-30 00:47:27 - browse：156

Sarepta - Cambridge -AP — Kristoffer Tripplaar/Sipa via AP

To hear Sarepta CEO Doug Ingram tell it, the results Monday afternoon from a large trial of its gene therapy for Duchenne muscular dystrophy marked a clear medical breakthrough. “A massive win,” he told investors, that could lead to its approval for all patients with the fatal muscle-wasting disease regardless of age.

And yet the rest of the Duchenne community was more cautious in its enthusiasm. The study — the most rigorous test to date of a technology 30 years in the making — had technically failed, as so many had before it.

“It’s extremely frustrating,” said John Brandsema, a pediatric neurologist at Children’s Hospital of Philadelphia who worked on the study. “When you spend decades trying to bring therapies into the clinic for something so severe and just keep missing over and over again.”

Get unlimited access to award-winning journalism and exclusive events.

Subscribe Log In

Previous article： Sports medicine is finally prioritizing gender equality
Next article： Key Senate committee drafts bipartisan bill to stem drug shortages

WSS

MultiPlan and major insurers sued for alleged medical price

Close Medicare's dangerous gaps in addiction treatment coverage

GOP presidential candidates start declaring their loyalty

MassMutual is introducing free genetic testing for members

Listen: Your guide to Wegovy's blockbuster heart study

H5N1 bird flu virus started spreading in cows in Texas in December

hotspot

leisure time

leisure time

How one medical school became remarkably diverse

Key Senate committee drafts bipartisan bill to stem drug shortages

Moonlake's readout produced a cash windfall. Risks remain

GOP presidential candidates start declaring their loyalty

Medical leaders decry Supreme Court decision on affirmative action

'Disease catastrophe' looms in Sudan as health conditions deteriorate, medics warn

Trump demands the U.S. pay no more for drugs than other countries … again

An innovative path out of biotech’s “valley of death”

Over 800 arrested across France in 3rd night of riots after fatal police shooting of teen

Kim Kardashian sparks debate on benefits of full

hotspot

UnitedHealth financials solid despite Change Healthcare cyberattack

The perfect storm of weather conditions that led to the devastating wildfires in Maui

Cue Health's Covid

Medical bills so high, Medicare adding extra digits to claim forms

Orangutan used medicinal plant to treat wound, first time ever seen

Orangutan used medicinal plant to treat wound, first time ever seen

leisure time

focus

hotspot

entertainment