fashion -WSS

fashion

author：fashion 2025-10-01 14:19:34 - browse：565

Two people run on the sugar-phosphate backbone of DNA while holding base pairs — in the lab coverage from STAT — Adobe

LONDON — Widespread genetic testing as well as the development of cutting-edge, customized genetic therapies have opened the door to treating many more inherited conditions than previously possible. A few recent cases, in which bespoke medicines were created for children with exceedingly rare mutations, have raised hopes for furthering the approach.

Now, researchers and government agencies in the U.K. are trying to figure out the nitty-gritty to replicate those early one-off successes for as many patients as possible — what sort of preclinical testing a tailor-made treatment needs to go through before being used, what regulatory thresholds each treatment needs to clear, and how to pay for these therapies.

“A lot of the barriers are no longer scientific — we can make these drugs,” said Matthew Wood, a professor of pediatrics at the University of Oxford. “It’s more about, can we make them at a cost that is reasonable enough? And can we get the regulators to reduce the barriers to doing this so that when a patient shows up, you can actually make a drug quickly enough to benefit that patient, rather than it costing huge amounts of money and taking two or three years to do it?”

Get unlimited access to award-winning journalism and exclusive events.

Subscribe Log In

Previous article： State Dept. review finds Biden bears some blame for Afghanistan failures
Next article： Bird flu outbreak in cows is latest avian flu curveball

entertainment

WSS

Dairy farmers resist CDC push for PPE against bird flu virus

Language on climate change, ESG removed from company website of Montana GOP Senate candidate

Suspects arrested after 3 women attacked on Manhattan's West Side: Police

Grand jury probing Trump's efforts to overturn 2020 election did not meet Friday: Sources

Why the advice to take all your antibiotics may be wrong

Google says AlphaFold 3 can map a vast universe of biomolecules

focus

fashion

focus

What does generative AI mean for health care? We asked experts

Why the advice to take all your antibiotics may be wrong

Supreme Court strikes down use of affirmative action

Grand jury probing Trump's efforts to overturn 2020 election did not meet Friday: Sources

Cancer drug shortages should be causing more outrage

Shionogi licenses Pompe disease therapy from Maze Therapeutics

Activists slam private health insurers over coverage restrictions

Biden White House, tech companies launch new safeguards around emerging AI technology

State Dept. review finds Biden bears some blame for Afghanistan failures

Study: People of West African ancestry at greater risk of cardiac amyloidosis

knowledge

After gene therapy, two congenitally deaf children hear for the first time

Florida babysitter arrested over hot car death, authorities say

Reframing the conversation around gain

Biden, Billy Joel, Elton John lead tributes for Tony Bennett after singer's death at 96

Shionogi licenses Pompe disease therapy from Maze Therapeutics

Biden White House, tech companies launch new safeguards around emerging AI technology

hotspot

hotspot

entertainment

explore