comprehensive -WSS

comprehensive

author：focus 2025-09-27 12:56:38 - browse：21

A young boy died in a trial for Pfizer’s experimental gene therapy for Duchenne muscular dystrophy, the company told patient advocates Tuesday.

The boy was enrolled in Daylight, a trial studying the treatment in boys aged 2 or 3. The boy had received the therapy early last year, Pfizer told the advocates in a note posted online by Parent Project Muscular Dystrophy.

Pfizer said the boy died of cardiac arrest, but that it was still working to understand what happened and the exact cause.

STAT+ Exclusive Story

Already have an account? Log in

This article is exclusive to STAT+ subscribers

Unlock this article — plus daily coverage and analysis of the pharma industry — by subscribing to STAT+.

Already have an account? Log in

Monthly

$39

Totals $468 per year

$39/month Get Started

Totals $468 per year

Starter

$30

for 3 months, then $39/month

$30 for 3 months Get Started

Then $39/month

Annual

$399

Save 15%

$399/year Get Started

Save 15%

11+ Users

Custom

Savings start at 25%!

Request A Quote Request A Quote

Savings start at 25%!

2-10 Users

$300

Annually per user

$300/year Get Started

$300 Annually per user

View All Plans

Get unlimited access to award-winning journalism and exclusive events.

Subscribe Log In

Previous article： After affirmative action ruling, medical educators look to 'holistic review'
Next article： Coercive sterilizations revealed by STAT prompt outrage

leisure time

WSS

Teladoc has a new CEO, but challenges remain the same

Deposition: Sackler embraced plan to conceal OxyContin’s strength

Sage considers ways to reduce costs following FDA rejection

Tuberculosis patients need more than just free medication

Lilly's Alzheimer's drug donanemab backed by FDA advisers

New report analyzes digital physical therapy solutions' effectiveness

focus

comprehensive

This article is exclusive to STAT+ subscribers

Unlock this article — plus daily coverage and analysis of the pharma industry — by subscribing to STAT+.

Wikipedia

Bright Health sells Medicare Advantage business to Molina

Flash flood warnings continue for parts of Missouri, Illinois

The Supreme Court will review a ruling striking down a domestic violence federal gun ban

Judge in Trump's classified documents case questions use of out

Biden outlines 'new path' to provide student loan relief after Supreme Court rejection

Moderna says combo Covid

Biden outlines 'new path' to provide student loan relief after Supreme Court rejection

NIH tests clinical research in primary care with $30 million program

Moonlake's readout produced a cash windfall. Risks remain

5 takeaways from STAT's examination of Zynex Medical

explore

Mexico finds 491 migrants being held at vacant lot, almost all are from Guatemala

Stephen Quake on the Chan Zuckerberg quest to conquer disease

Doctors push to include dialysis machines in emergency stockpile