knowledge -WSS

knowledge

author：fashion 2025-09-28 02:47:28 - browse：2

Here is STAT’s biotech scorecard, our regular ledger of stock-moving biotech events, for the fourth quarter:

The Food and Drug Administration’s decision in June to grant conditional approval to a gene therapy for Duchenne muscular dystrophy was a watershed moment for the treatment of the neuromuscular disease, and a big win for its maker, Sarepta Therapeutics. Confirming the gene therapy’s benefit — and potentially broadening its use to include older boys — will be determined by a Phase 3 clinical trial that will read out later this quarter.

Pfizeris developing its own gene therapy for Duchenne in a fully enrolled Phase 3 study with final results expected in 2024. But before the verdict is revealed, Pfizer intends to conduct an interim analysis later this quarter. The most likely outcome of this early look will be a determination to continue the study to its completion. But surprises — including an early stop for overwhelming efficacy — can’t be ruled out.

Get unlimited access to award-winning journalism and exclusive events.

Subscribe Log In

Previous article： Anesthesiologist group: stop taking Ozempic before surgery
Next article： ADA: All diabetes patients should be screened for liver condition

hotspot

leisure time

WSS

Judge in Trump's classified documents case questions use of out

The simple reason for the increase in autism diagnosis

Severe weather updates: 1 million customers without power in 11 states as storms pummel East Coast

Synthetic human embryos? Researchers say term is overblown

With heat waves through August, officials warn of health risks

How CRISPR works, explained in two minutes

hotspot

knowledge

hotspot

Malaria cases in Florida and Texas: Here’s what you need to know

Belarusian journalist sentenced to 4 years in prison as crackdown continues

In Memoriam: Notable people who died in 2023

Anger, defiance, fear over Supreme Court decision to block student loan forgiveness

At least 13 dead in Texas as scorching temps continue

Supreme Court rules employers must be more accommodating of religious observance

Over 800 arrested across France in 3rd night of riots after fatal police shooting of teen

Many breast cancer patients receive more radiation than needed

Wildfire smoke exposes gaps in outdoor worker protections

Illumina to lay off 10% of research and development team

entertainment

UnitedHealth wins $3.3 billion takeover of Amedisys

Lilly’s obesity pill cuts 15% of weight at highest dose in mid

Why do we get seasonal allergies?

UnitedHealth starts bidding war with $3.3 billion offer for Amedisys

St. Louis police protesters begin picking up checks in $4.9 million settlement

Wildfire smoke map: Which US cities are forecast to be impacted by fires burning in Canada

explore

hotspot

leisure time

Wikipedia