explore -WSS

explore

author：Wikipedia 2025-09-03 14:38:43 - browse：58257

Illustration of two DNA strands made of banknotes. -- health coverage from STAT — Adobe

The staff of the Institute for Clinical and Economic Review, or ICER, are known as the nerds of the drug industry: bespectacled killjoys who emerge a few times a year to scold drugmakers for pricing their latest cancer or MS advance far beyond reason.

But last year, they sat down and concluded a forthcoming treatment was worth up to $3.9 million — more than any medicine in history, more than a 45-year supply of Humira, the autoimmune drug often held up as an emblem of America’s runaway drug spending.

It was a testament to the power of a new class of gene therapies to deliver something pharma so rarely does: Genuine cures. The treatment, approved last week as Lenmeldy, may allow some babies born with an ultra-rare neurodegenerative disease called metachromatic leukodystrophy, or MLD, to grow up and live essentially normal lives.

Get unlimited access to award-winning journalism and exclusive events.

Subscribe Log In

Previous article： Medicare details structure of new drug price negotiation program
Next article： The Harvard botanist who searched for psychedelics in the Amazon

WSS

Violet CEO on training clinicians to promote more inclusive care

Neurocrine Biosciences, biotech based in San Diego, joins PhRMA

Grail spinoff by Illumina should end disastrous merger attempt

Neurocrine Biosciences, biotech based in San Diego, joins PhRMA

Ed Silverman on new gene therapies, biosimilars, coffee, and more

Advocates call out 'SNL' over stereotypes, errors in sickle cell skit

leisure time

explore

Wikipedia

At least 13 dead in Texas as scorching temps continue

Hospitals owned by private equity see complications spike 25%

Dobbs anniversary: the lost opportunity of abortion as health care

Keeping primary care docs in field isn't impossible, says AAFP CEO

United colonoscopy coverage change 'may cost lives,' doctors say

Carvykti CAR

Sports medicine is finally prioritizing gender equality

In Spain, a hospital brews its own CAR

Wildfire smoke exposes gaps in outdoor worker protections

Drinking less cuts risk of oral cavity, esophageal cancer: Report

focus

With competition flaring, obesity drug hits goal in liver disease study

CRISPR gene editing developments we’re watching in 2024

Readout LOUD podcast: Humira legacy, AbbVie CEO's retirement

A solution to the after

Virtual care provider acquires bankrupt Pear's prescription apps

Why health records don't always know when patients are dead

Wikipedia

focus

focus

Wikipedia