entertainment -WSS

entertainment

author：entertainment 2025-09-03 07:44:05 - browse：2

The FDA building -- First Opinion coverage from STAT — Adobe

U.S. regulators on Wednesday approved the first treatment for an ultra-rare disease that causes people to grow bone where it otherwise shouldn’t be, extending an option to patients who have been advocating for access to the medicine.

The treatment, an oral medication that will be marketed as Sohonos, faced some questions about the quality of its data, and was rejected earlier this year by European regulators. But in approving the drug for the treatment of fibrodysplasia ossificans progressiva, or FOP, the Food and Drug Administration concluded that Sohonos’ benefits outweigh its risks.

“I just closed my eyes and looked up to the skies, like ‘Thank you, God,’” said Suzanne Hollywood, whose teenage son, Joey, has been receiving the drug in a clinical trial. “It’s far from perfect, but I’m thrilled for my son, for his future, and for the kids getting diagnosed who might not have to experience what others had to.”

Unlock this article by subscribing to STAT+ and enjoy your first 30 days free!

GET STARTED Log In

Previous article： Tori Bowie and the unacceptable rates of Black maternal death
Next article： Johnson & Johnson sued for allegedly overpaying for workers' drugs

explore

WSS

AstraZeneca stays mum on Medicare drug pricing negotiations

Problems with a popular proposal to regulate AI in health care

Nearly two

Texas Medical Board asked to define abortion emergency exception

Nearly two

Trump drops motion seeking removal of DA probing efforts to overturn 2020 election in Georgia

knowledge

entertainment

focus

After affirmative action ruling, medical educators look to 'holistic review'

The drug industry sees a key ally in the Senate prevail

United colonoscopy coverage change 'may cost lives,' doctors say

What the cancer research community can learn from the Covid response

How one medical school became remarkably diverse

A cyberattack has disrupted hospitals and health care in several states

In Memoriam: Notable people who died in 2023

Nearly two

Apple is now the first public company to be valued at $3 trillion

Novo Holdings to buy drug manufacturer Catalent in $16.5B deal

Wikipedia

Biden calls for immediate release of Niger's president amid apparent coup

ProMED, early warning system on disease outbreaks, in peril

Readout LOUD: Venture capital, Gilead, and more M&A

Global cancer cases to surge 77% by 2050, WHO report says

The Biogen Aduhelm mess could happen again

Padmanee Sharma of MD Anderson at center of lawsuit over credit

hotspot

explore

entertainment

hotspot