entertainment -WSS

entertainment

author：focus 2025-09-02 22:06:58 - browse：7192

Colorful broken DNA helix genome. -- health coverage from STAT — Adobe

In 2020, as biotech stocks surged amid the pandemic, a startup called Taysha Gene Therapies raised over $300 million off an audacious promise: It was going to license and develop gene therapies for at least 18 different rare and serious neurological diseases.

The effort brought hope for many rare disease families, some of whom had raised money to fund the UT-Southwestern scientist who designed the treatments after they saw no other options for their children.

Last week, the grand plan took perhaps a final blow. Taysha announced it would discontinue development of a treatment for giant axonal neuropathy, or GAN, a fatal, degenerative disease known to affect fewer than 100 people worldwide. The FDA, Taysha said, had requested an additional clinical trial that would be infeasible.

Get unlimited access to award-winning journalism and exclusive events.

Subscribe Log In

Previous article： Jerome Adams on the need for new antivirals for Covid
Next article： Readout Newsletter: Merck, Vertex, and Viking updates

leisure time

Wikipedia

WSS

The Readout: Lenmeldy, GLP

Late stage cancers on the rise after pandemic delayed screenings

Readout LOUD podcast: mifepristone case, GLP

2 officers injured in shooting in Orlando, police say

Florida officials tell state schools to teach AP Psychology 'in its entirety'

Primary care physicians play key roles in Alzheimer's management

hotspot

entertainment

Wikipedia

Anesthesiologist group: stop taking Ozempic before surgery

Biotech startup Celsius cuts 75% of staff ahead of first trial start

Drug repurposing or repositioning? The language matters

Pharma showers House GOP doctor with campaign cash

Moonlake's readout produced a cash windfall. Risks remain

Patient advocates debate FDA's accelerated approval process

Virginia high school admissions case could be legal follow

Patient advocates debate FDA's accelerated approval process

New Eli Lilly Alzheimer’s data poses Medicare coverage conundrum

Chris Christie meets with Zelenskyy during Ukraine trip

leisure time

Patient advocates debate FDA's accelerated approval process

Heart disease in astronauts blamed on cosmic radiation

Judge partially blocks Texas abortion ban for medical emergencies, fatal diagnoses

FDA's naming rule on biosimilars has undermined competition

Florida officials tell state schools to teach AP Psychology 'in its entirety'

Heart disease in astronauts blamed on cosmic radiation

knowledge

leisure time

Wikipedia

focus