explore -WSS

explore

author：Wikipedia 2025-08-06 04:47:09 - browse：52

Gene therapy helped Conner Curran, right, walk, but as the drug fades, his family is supporting scientific efforts to allow him and other boys get a second dose. -- Biotech coverage from STAT — Gene therapy helped Conner Curran (at right) walk, but as the drug fades, his family is supporting scientific efforts to allow him and other boys get a second dose. Courtesy Jess & Chris Curran

In the beginning, Conner Curran ran up the stairs.

It was a miraculous moment for him and his parents, Jess and Chris Curran. Just months before, contractors were in their New York home to install a motorized lift, while Jess tearfully explained that it wasn’t for a grandparent but for their 7-year-old son, who suffered from Duchenne muscular dystrophy and could barely haul himself up the steps.

Then Conner was accepted as the first patient in Pfizer’s Duchenne gene therapy trial. Three weeks later, he could bound to the second floor. Soon, he could walk the two-plus miles to Goldberg’s, a local bagel shop. “I couldn’t do that before,” he told NPR in 2020.

Unlock this article by subscribing to STAT+ and enjoy your first 30 days free!

GET STARTED Log In

Previous article： New Eli Lilly Alzheimer’s data poses Medicare coverage conundrum
Next article： Why the advice to take all your antibiotics may be wrong

leisure time

WSS

Prosecutors say FTX founder Sam Bankman

A former Republican legislative candidate has been charged for his role in the US Capitol riot

Biden, Billy Joel, Elton John lead tributes for Tony Bennett after singer's death at 96

Unmasking the 'centricity' illusion in clinical trials

The biotech scorecard for the 2nd quarter: 12 industry events to watch

Language on climate change, ESG removed from company website of Montana GOP Senate candidate

entertainment

explore

Wikipedia

The cancer drug shortage isn’t new — and neither are the solutions

Washington Commanders' Dan Snyder ordered to pay NFL $60M following investigation

At least 13 dead in Texas as scorching temps continue

New research sheds light on how often breast cancer is overdiagnosed

Indiana Supreme Court upholds abortion ban, says state constitution gives only limited protections

Asahi Kasei to buy Calliditas, picking up kidney disease drug

New Eli Lilly Alzheimer’s data poses Medicare coverage conundrum

Mega Millions jackpot grows to $720 million ahead of Friday's drawing

How one medical school became remarkably diverse

Lawsuit challenges CMS nursing home minimum staffing rule

Wikipedia

What is the Turing Test that determines if computers can think?

A former Republican legislative candidate has been charged for his role in the US Capitol riot

Listen: BridgeBio's big week & Lilly's Alzheimer's data

New chart reveals military’s vast involvement in Operation Warp Speed

Biden White House, tech companies launch new safeguards around emerging AI technology

Decentralized clinical trials need collaboration to achieve wider use

focus

leisure time

Wikipedia

entertainment